International Niemann–Pick Disease Alliance

Adrabetadex 2021: webinar featuring Dr. Porter and Dr. Berry-Kravis discussing the Adrabetadex Program

You can find the video recording from the Ara Perseghian Medical Research Fund’s February 3, 2021 webinar below, where Dr. Elizabeth Berry-Kravis and Dr. Denny Porter presented their Expanded Access Program data, Natural History Data, and recent longitudinal data analysis for the Adrabetadex program:

You can also view the video recording from the previous January 22, 2021 webinar where Mallinckrodt Pharmaceuticals presented their reasoning behind the discontinuation of the Adrabetadex program, here.

 

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