International Niemann–Pick Disease Alliance
You can find the video recording from the Ara Perseghian Medical Research Fund’s February 3, 2021 webinar below, where Dr. Elizabeth Berry-Kravis and Dr. Denny Porter presented their Expanded Access Program data, Natural History Data, and recent longitudinal data analysis for the Adrabetadex program:
You can also view the video recording from the previous January 22, 2021 webinar where Mallinckrodt Pharmaceuticals presented their reasoning behind the discontinuation of the Adrabetadex program, here.