International Niemann–Pick Disease Alliance

First European site is now recruiting for VTS-270 trial in NP-C

Great news for the NP-C community – the first European trial site for VTS-270 (2-hydroxypropyl-β-cyclodextrin) for Niemann-Pick Type C1  is now recruiting! Professor Marquardt of the Universitätsklinikum in Münster is the investigator contact for this location:

Thorsten Marquardt, Univ. Prof. Dr.
+49 2518356494

For more information please visit or the trial website developed by Vtesse at We’re delighted that a European site has started to recruit – in addition to the 4 sites already activated in the USA – and look forward to further announcements soon.

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