International Niemann–Pick Disease Alliance
INPDA member Niemann-Pick UK provides a new post from Will Evans (father of Sam, NP-C, and trustee of NPUK), giving his perspective of the planned clinical trials in NP-C:
New Post! Clinical Trials in NP-C – My Perspective, by Dr.William Evans
So two trials for NP-C in 2015 have been announced, but what do we know about each…?
Earlier this year, we ran a series of posts from NP-UK Trustee, Dr. William Evans, father of Sam, age 7, NP-C. In his new post, Will provides his thoughts on Vtesse, Orphazyme and their clinical trials. Please click on the link below to read the post; you can send your questions or comments to firstname.lastname@example.org and we will pass these along to Will.
You can read Will’s previous posts here: