International Niemann–Pick Disease Alliance
Niemann-Pick Disease Awareness Month is the perfect time to acknowledge the invaluable role that siblings play in providing support and love to their affected family members. Cuando Alejandro tenía 2 añitos, llegó al mundo su hermana tan esperada, Natalia....
As part of this year’s Niemann-Pick Disease Awareness Month, we are putting the spotlight on siblings as we feel they are often a huge support to both their brother or sister, as well as the broader family. They are also some...
As part of this year’s Niemann-Pick Disease Awareness Month, we are putting the spotlight on siblings as we feel they are often a huge support to both their brother or sister, as well as the broader family. They are also some...
As part of this year’s Niemann-Pick Disease Awareness Month, we are putting the spotlight on siblings as we feel they are often a huge support to both their brother or sister, as well as the broader family. They are also some...
Combined company will operate as Cyclo Therapeutics with primary focus on advancing Trappsol® Cyclo™ for the treatment of Niemann-Pick Disease Type C1 (NPC1) At closing combined Company will have approximately $13.7 million cash on hand to fund operations into 2H...
Celebrating Strength and Support during NPD Awareness Month… …let’s shine a bright light on the unsung heroes of our Niemann-Pick Disease (NPD) community this October, during Niemann-Pick Disease Awareness Month. We’re thrilled to introduce our “Sibling Spotlight” campaign, dedicated...
– Data published in official journal of Molecular Genetics and Metabolism Reports: Evidence of a change in cholesterol homeostasis in peripheral organs and the brain after the initial infusion Trappsol® Cyclo™ was detected in the CSF Completers had an 88.9% improvement...
– Phase 3 trial met the primary endpoint and key secondary endpoints showing high statistical significance – IB1001 showed a clinically meaningful improvement in symptoms, functioning, quality of life, and cognition in both pediatric and adult patients with NPC...