International Niemann-Pick Disease Alliance (INPDA)

Orphazyme A/S under In-Court-Restructuring to sell substantially all of its assets and business activities to KemPharm, Inc.

Orphazyme A/S in restructuring Company announcement No. 24/2022 Inside information www.orphazyme.com Company Registration No. 32266355 KemPharm to acquire Orphazyme assets,...
Read story
Pfrieger’s Digest – 06/2022 Edition

“Pfrieger’s Digest” is written by Frank Pfrieger of Niemann-Pick Selbsthiifegruppe (Germany) to provide an overview of the latest advances in Niemann-Pick...
Read story
Webinar: The impacts of olipudase alfa on pediatric patients with ASMD and their families

We are pleased to be able to share the following collaborative webinar entitled The impacts of olipudase alfa on pediatric...
Read story

Rare Disease Day (RDD) 2023
- Event date: 28.02.23
View event info

View all events