A global network of non-profit organisations supporting those affected by Niemann-Pick diseases.

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Xenpozyme Supply Update

INPDA has been informed by Sanofi of supply interruptions affecting Xenpozyme (olipudase alfa), a treatment for Acid Sphingomyelinase Deficiency...

Cyclo Therapeutics Announces Submission of New Drug Application to FDA for Trappsol® Cyclo™ (remibetadex) for the Treatment of Niemann-Pick Disease Type C

October 29, 2026 Dear NPC Organizational Leaders, As we approach the conclusion of Niemann-Pick Disease Awareness Month, we are...

Cyclo Therapeutics Provides Update on Trappsol® Cyclo™ Development Programme