International Niemann-Pick Disease Alliance (INPDA)

Orphazyme provides regulatory update following Type A meeting with FDA on arimoclomol in Niemann-Pick disease type C

Progress made in understanding potential resolution of topics outlined in Complete Response Letter, including need for additional data to...
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Orphazyme provides regulatory and financial updates

Copenhagen – October 5, 2021 – Orphazyme A/S (ORPHA.CO; ORPH), a late-stage biopharmaceutical company, today announces regulatory updates for...
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Cyclo Therapeutics Appoints Lise Lund Kjems, MD, PhD as Chief Medical Officer

Sep 27, 2021 – Dr. Kjems is a leading global physician scientist with a proven pharma track record of...
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