International Niemann–Pick Disease Alliance

Calporta Therapeutics is developing small molecule agonists of TRPML1 for Niemann-Pick C

Calporta Therapeutics is developing small molecule agonists of TRPML1 for the treatment of Niemann-Pick C Disease (NPC) and other lysosomal storage diseases. Calporta’s approach is based on research from the lab of Haoxing Xu, Ph.D., at the University of Michigan.

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