International Niemann–Pick Disease Alliance

Trials: A Desperate Fight to Save Kids & Change Science

For six years, The Wall Street Journal followed a group of parents and scientists seeking a treatment for a rare and fatal genetic disease that strikes primarily children. Their collaboration accelerated development of a promising drug and, along the way, pushed the boundaries of medical research itself.

Follow this link to learn more about the story associated with Niemann-Pick Disease Type C:

http://projects.wsj.com/trials/#chapter=1

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Think Again. Think NP-C

Join our international campaign to improve diagnosis of NP-C!