International Niemann–Pick Disease Alliance

Orphazyme’s Prospective Non-therapeutic Study in Patients Diagnosed With NP-C

Orphazyme’s ‘Observational’ study for NP-C has been registered and made available on www.clinicaltrials.gov. The trial identifier is NCT02435030. Confirmed sites and contact details are provided.

https://clinicaltrials.gov/ct2/show/NCT02435030?term=arimoclomol&rank=5

You can find further information on Orphazyme’s website www.orphazyme.com

 

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