International Niemann–Pick Disease Alliance

Updates

  1. Cyclo Therapeutics, Inc. to Present Clinical Trial Data on Niemann-Pick type C Disease at the 16th Annual WORLDSymposium

    Data show that Trappsol® Cyclo™, the Company’s proprietary hydroxypropyl beta cyclodextrin drug, reduces levels of trapped cholesterol in liver tissue of Niemann-Pick Disease Type C Patients GAINESVILLE, FL – (Businesswire) – December 16, 2019 – Cyclo Therapeutics, Inc. (OTCQB:...

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  2. Orphazyme receives Breakthrough Therapy Designation for arimoclomol in Niemann-Pick Disease Type C (NPC)

    Orphazyme receives Breakthrough Therapy Designation for arimoclomol in Niemann-Pick Disease Type C (NPC) • There are currently no US FDA-approved products for NPC • Orphazyme plans to file arimoclomol in the US in H1 2020 Copenhagen, Denmark, November 19,...

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  3. Cyclo Therapeutics Announces Its Publication of the Most Extensive Set of Case Study Reports To-date on Expanded Access Use of Hydroxypropyl Beta Cyclodextrin in Niemann-Pick Disease Type C

    Publication describes favorable safety profile and efficacy in neurologic and other disease features in individual NPC patients following intravenous administration of drug Gainesville, FL – (Businesswire) – 31 October 2019 – Cyclo Therapeutics, Inc, (OTCQB: CTDH), a clinical stage...

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  4. Cyclo Therapeutics Announces Completion of Enrollment in its Phase I Trial to Evaluate Trappsol® Cyclo™ for the Treatment of Niemann-Pick Disease Type C

    Top line results are expected to be available in February 2020 GAINESVILLE, FL – (Businesswire) – October 22, 2019 – Cyclo Therapeutics, Inc. (OTCQB: CTDH), formerly CTD Holdings, Inc., a biotechnology company that develops cyclodextrin-based products for the treatment...

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  5. Cyclo Therapeutics Announces Its Support for The Firefly Fund’s Newborn Screening Program

    Announcement made in conjunction with October 19th Global Awareness Day for Niemann-Pick Disease sponsored by International Niemann Pick Disease Alliance GAINESVILLE, FL – (Businesswire) – October 18, 2019 – Cyclo Therapeutics, Inc. (OTCQB: CTDH), formerly CTD Holdings, Inc., a...

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  6. CTD Holdings Announces FDA Approval of US Expanded Access Treatment Program in Niemann-Pick Disease Type C

    ALACHUA, FL–(Businesswire)–13 September 2019–CTD Holdings, Inc. (OTCQB: CTDH), a clinical stage biotechnology company that develops cyclodextrin-based products for the treatment of disease with unmet medical need, today announced that the company will provide Trappsol® Cyclo™, its proprietary hydroxypropyl beta...

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  7. IntraBio: Clinical Trial IB1001-201: US Recruitment

    Inc. is pleased to confirm that the Clinical Trial IB1001-201, “Effects of N-Acetyl-L-Leucine on Niemann-Pick type C Disease (NPC): A multinational, multi-center, open-label, rater-blinded Phase II study” is open for recruitment in the United Kingdom. IB1001-201 is a multinational...

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  8. CTD Holdings to Present at 2019 Annual Conference for NPC Patients, Families, and Health Professionals in the United Kingdom

    CTD is also a proud sponsor of the conference, for the 4th year running… ALACHUA, FL–(Businesswire)–11 September 2019–CTD Holdings, Inc. (OTCQB: CTDH), a clinical stage biotechnology company that develops cyclodextrin-based products for the treatment of disease with unmet medical...

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  9. ORPHAZYME ANNOUNCES INTERIM REPORT FIRST HALF 2019

    Copenhagen, Denmark, August 28, 2019 – Orphazyme A/S (ticker: ORPHA.CO), a biopharmaceutical company dedicated to developing treatments for patients living with rare diseases, today announces its interim financial results for the period January 1 – June 30, 2019 and corporate highlights. “We have made...

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  10. CTD Announces New Data Presented at Annual Gathering of Patients and Families Tackling Niemann-Pick Disease Type C

    CTD presentation to take place at the National Niemann-Pick Disease Foundation Conference August 16, 2019 ALACHUA, FL – (Businesswire) – August 14, 2019 – CTD Holdings, Inc. (OTCQB: CTDH), a clinical stage biotechnology company that develops cyclodextrin-based products for...

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